Alnylam Pharmaceuticals

E100609

Alnylam Pharmaceuticals is a biopharmaceutical company specializing in the development of RNA interference (RNAi)-based therapeutics for genetically defined diseases.

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Predicate Object
instanceOf biopharmaceutical company
public company
collaboratesWith Novartis
Regeneron Pharmaceuticals
Roche
Sanofi
Vir Biotechnology
country United States of America
surface form: United States
develops Amvuttra
Givlaari
Onpattro
Oxlumo
focusesOn cardiometabolic diseases
central nervous system diseases
hepatic infectious diseases
rare genetic diseases
foundedBy David Bartel
John Maraganore
Paul Schimmel
Phil Zamore
Phillip A. Sharp
Thomas Tuschl
hasClinicalStagePrograms ATTR amyloidosis
cardiovascular disease
hemophilia
hypercholesterolemia
hypertension
hasIndication acute hepatic porphyria
hereditary transthyretin-mediated amyloidosis
polyneuropathy of hereditary transthyretin-mediated amyloidosis
primary hyperoxaluria type 1
hasSubsidiary Alnylam Pharmaceuticals self-linksurface differs
surface form: Alnylam Pharmaceuticals Ireland
headquartersLocation Cambridge, Massachusetts
surface form: Cambridge, Massachusetts, United States
inception 2002
industry biotechnology
pharmaceuticals
listedOn NASDAQ
missionStatement to transform the lives of patients with RNAi therapeutics
productType RNAi therapeutic
researchArea gene silencing
siRNA therapeutics
specializesIn RNA interference therapeutics
RNAi-based drugs for genetically defined diseases
targetOrgan liver
technologyPlatform RNA interference
tickerSymbol ALNY
usesDeliveryTechnology GalNAc conjugate delivery
website https://www.alnylam.com

Referenced by (2)

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Phillip A. Sharp coFounded Alnylam Pharmaceuticals
Alnylam Pharmaceuticals hasSubsidiary Alnylam Pharmaceuticals self-linksurface differs
this entity surface form: Alnylam Pharmaceuticals Ireland