exagamglogene autotemcel

E1188107 UNEXPLORED

Exagamglogene autotemcel is an investigational CRISPR/Cas9-based gene-editing therapy being developed to treat inherited blood disorders such as sickle cell disease and transfusion-dependent beta thalassemia.

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exagamglogene autotemcel canonical 1

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Vertex Pharmaceuticals hasClinicalProgram exagamglogene autotemcel