AveXis
E564274
AveXis is a biotechnology company best known for developing the gene therapy onasemnogene abeparvovec (Zolgensma) for spinal muscular atrophy.
Observed surface forms (3)
| Surface form | Occurrences |
|---|---|
| onasemnogene abeparvovec | 0 |
| Zolgensma | 0 |
| Novartis Gene Therapies | 0 |
Statements (44)
| Predicate | Object |
|---|---|
| instanceOf |
biotechnology company
ⓘ
gene therapy ⓘ |
| acquiredBy | Novartis NERFINISHED ⓘ |
| acquisitionDate | 2018 ⓘ |
| acquisitionValue | 8770000000 USD ⓘ |
| approvalDate |
2019
ⓘ
2019 ⓘ |
| approvedBy |
U.S. Food and Drug Administration
NERFINISHED
ⓘ
U.S. Food and Drug Administration NERFINISHED ⓘ |
| changedNameTo | Novartis Gene Therapies NERFINISHED ⓘ |
| chiefExecutiveOfficer | Sean Nolan NERFINISHED ⓘ |
| clinicalTrialPhase | Phase 3 (for SMA gene therapy prior to approval) ⓘ |
| collaboratedWith | Nationwide Children’s Hospital NERFINISHED ⓘ |
| country |
United States of America
ⓘ
surface form:
United States
|
| developed |
Zolgensma
NERFINISHED
ⓘ
onasemnogene abeparvovec NERFINISHED ⓘ |
| focusesOn |
neuromuscular disorders
ⓘ
rare diseases ⓘ spinal muscular atrophy ⓘ |
| formerName | Biolife Cell Bank NERFINISHED ⓘ |
| foundedBy |
Brian Kaspar
NERFINISHED
ⓘ
John Carbona NERFINISHED ⓘ Sean Nolan NERFINISHED ⓘ |
| headquartersLocation | Bannockburn, Illinois NERFINISHED ⓘ |
| indication |
spinal muscular atrophy
ⓘ
spinal muscular atrophy ⓘ |
| industry |
biotechnology
ⓘ
gene therapy ⓘ |
| listedOn | NASDAQ ⓘ |
| parentOrganization |
Novartis
NERFINISHED
ⓘ
Novartis NERFINISHED ⓘ |
| product |
Zolgensma
NERFINISHED
ⓘ
onasemnogene abeparvovec NERFINISHED ⓘ |
| receivedApprovalFor | onasemnogene abeparvovec NERFINISHED ⓘ |
| regulatoryApproval | U.S. Food and Drug Administration NERFINISHED ⓘ |
| researchFocus |
central nervous system disorders
ⓘ
genetic neuromuscular diseases ⓘ |
| specializesIn | AAV-based gene therapies ⓘ |
| status | subsidiary of Novartis ⓘ |
| technology | adeno-associated virus vector ⓘ |
| therapeuticArea | gene replacement therapy ⓘ |
| tickerSymbol | AVXS NERFINISHED ⓘ |
| tradeName | Zolgensma NERFINISHED ⓘ |
| usesVector | AAV9 NERFINISHED ⓘ |
Referenced by (1)
Full triples — surface form annotated when it differs from this entity's canonical label.