Committee for Orphan Medicinal Products

E24718

The Committee for Orphan Medicinal Products is a specialized expert body that evaluates and advises on the designation and development of medicines for rare diseases within the European Union.

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Statements (47)

Predicate Object
instanceOf European Union body
expert body
regulatory advisory committee
scientific committee
abbreviation COMP
appliesTo human medicinal products
collaboratesWith European Commission
national competent authorities of EU Member States
patient organizations
pharmaceutical industry
composition experts in rare diseases and orphan drugs
members nominated by EU Member States
members nominated by the European Commission
patient representatives
country European Union
field drug development
orphan medicinal products
pharmaceutical regulation
rare diseases
focus conditions affecting not more than 5 in 10,000 people in the EU
goal facilitate development and availability of orphan medicines in the EU
improve treatment options for patients with rare diseases
grants opinions that can lead to market exclusivity incentives
inception 2000
jurisdiction European Union
language English
legalBasis Regulation (EC) No 141/2000
Regulation (EC) No 726/2004
locatedIn Amsterdam
Netherlands
meetsAt European Medicines Agency headquarters
parentOrganization European Medicines Agency
partOf European Medicines Agency
provides scientific advice on orphan drug development strategies
regulates orphan medicinal product designation in the EU
role advise on development of medicines for rare diseases
advise the European Commission on orphan medicinal products
contribute to guidelines on orphan drug development
evaluate applications for orphan designation of medicines
provide opinions on orphan medicinal product designation
support implementation of EU orphan drug legislation
subjectOf EU orphan drug policy
typeOfJurisdiction supranational
website https://www.ema.europa.eu/en/committees/committee-orphan-medicinal-products-comp
worksOn orphan designation procedures
protocol assistance for orphan medicines
review of maintenance or withdrawal of orphan designation

Referenced by (3)

Full triples — surface form annotated when it differs from this entity's canonical label.

Regulation (EC) No 726/2004 establishes Committee for Orphan Medicinal Products
this entity surface form: Committee for Orphan Medicinal Products within the European Medicines Agency
European Medicines Agency hasCommittee Committee for Orphan Medicinal Products
EMA hasCommittee Committee for Orphan Medicinal Products
subject surface form: European Medicines Agency